Special Offer: Free Regulatory Strategy Consultation for Research Institutes Working on Children’s Rare Diseases
Building Hope for Children with Rare Health Conditions
We care about all children who have rare diseases.
Funding Research Labs Across the US that Focus on Rare Children’s Diseases
Combined Federal Campaign-Approved Charity
Combined Federal
Campaign -Approved Charity
Advancing Research in Children's Rare Diseases
The Children’s Rare Disease Organization champions the pursuit of knowledge to unlock the mysteries of rare diseases afflicting young lives and their families. We are steadfast in supporting innovative research in children’s rare diseases, enhancing public awareness, and nurturing a future where every child can thrive, unrestricted by the challenges of illnesses.
Unwavering Support for Groundbreaking Research
With pride, we’ve catalyzed scientific exploration through financial support to research labs and institutions across the country, like Georgetown University and the University of Colorado. Our initiatives are making strides in understanding liver fibrosis, among other rare diseases, propelling us closer to discovering effective treatments and potential cures.
Awareness: The Catalyst for Enhanced Research and Progress
Stepping into the light of awareness, we stand at the forefront of revolutionizing the care for children’s rare diseases. By amplifying knowledge and nurturing empathy, we knit together a community dedicated to significantly uplifting afflicted young lives.
Our mission is fueled by the insights and expertise of our Board of Directors, a team of eminent professionals with Ph.D.s and M.D.s. They draw from over two decades of experience in drug development across manufacturing, nonclinical, and clinical spectrums. Their unparalleled ability to assess research proposals ensures that we back pioneering studies poised for breakthroughs in treatment.
Learn more about how we advance research in children’s rare diseases.
A Dedication to Groundbreaking Solutions and Unwavering Support
Operating as a 501(c)(3) nonprofit organization, we are steered by integrity and a shared purpose. Our Board consists of volunteers, distinguished by their commitment and without personal compensation, all united in navigating paths to discovery and cure. With our collective expertise, we offer comprehensive support in druggability strategies, manufacturing, nonclinical proof of concept, toxicity studies, clinical design, and navigating regulatory pathways.
Our commitment extends to offering free research funds to accelerate the pace of finding cures. Your support transforms into direct action, empowering us to provide regulatory consulting and vital resources for developing treatments for conditions like Biliary Atresia, all at no cost. Together, we embark on a journey toward achieving the ultimate goal of successful rare disease treatments, elevating the standard of care and hope for children and their families worldwide.
Join Our Cause
We invite you to stand with us. Whether you’re an individual or an organization keen on making a palpable difference, your donation to the Children’s Rare Disease Organization is a powerful statement of hope for children affected by rare diseases. Reach out and become a part of the solution to meet every patient’s medical needs. Send us a message for additional information.